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Italy, USA, Genetics
Renewed hope for gene therapy in rare disease
Renewed hope for gene therapy in rare disease Between 30 and 40 million people in Europe suffer from rare diseases —many of them children. As most of these diseases have genetic origins, gene therapy is a major hope for their future cure .
Two approaches to treat Lysosomal Storage Diseases
Two approaches to treat Lysosomal Storage Diseases Lysosomes are membrane-bound organelles found in most animal cells. They are responsible for treating cellular waste. Genetic mutations in lysosomal enzymes lead to lysosome malfunction and waste accumulation.
Huntington's disease: A treatment in sight?
Huntington's disease: A treatment in sight? A treatment to directly fight Huntington’s disease could finally be in sight . Until now, therapies for this severely debilitating genetic disorder have only focused on alleviating physical and psychiatric symptoms.
Anti-allergy GM apples
Anti-allergy GM apples Peanut, egg and soy are more common food known to trigger an allergic reaction, a problem affecting around 8% of children in the EU. Intuitively, you might not list apples as causing allergic reactions.